January 09, 2012
Interview with Samuel G. Jacobson, MD, PhD, author of Gene Therapy for Leber Congenital Amaurosis Caused by RPE65 Mutations: Safety and Efficacy in 15 Children and Adults Followed Up to 3 Years
ARTICLE: Gene Therapy for Leber Congenital Amaurosis Caused by RPE65 Mutations: Safety and Efficacy in 15 Children and Adults Followed Up to 3 Years
Arch Ophthalmol. Published online January 01, 2012. doi:10.1001/archophthalmol.2011.298
Samuel G. Jacobson, MD, PhD; Artur V. Cideciyan, PhD; Ramakrishna Ratnakaram, MD; Elise Heon, MD; Sharon B. Schwartz, MS, CGC; Alejandro J. Roman, MS; Marc C. Peden, MD; Tomas S. Aleman, MD; Sanford L. Boye, MS; Alexander Sumaroka, PhD; Thomas J. Conlon, PhD; Roberto Calcedo, PhD; Ji-Jing Pang, MD, PhD; Kirsten E. Erger, BS; Melani B. Olivares, BA; Cristina L. Mullins, BA; Malgorzata Swider, PhD; Shalesh Kaushal, MD, PhD; William J. Feuer, MS; Alessandro Iannaccone, MD, MS; Gerald A. Fishman, MD; Edwin M. Stone, MD, PhD; Barry J. Byrne, MD, PhD; William W. Hauswirth, PhD
7:33
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